Friday, July 10, 2026

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Blueprint Medicines

Blueprint Medicines drug portfolio — 9 indexed compounds with therapeutic class and molecular targets from public FDA and regional approval metadata.

Cambridge, USA HQ
2011 Founded
741 Employees
EMA registrant Type
Company details
Status
Public
HQ
Cambridge, USA
Founded
2011
Employees
741
Programs
8
Drugs
9
Patents
0
Intelligence · Drug Pipeline

Blueprint Medicines pipeline

Portfolio lens on 9 drugs and development assets — regulatory status, targets, and deep links to NovaPharmaNews drug profiles.

Blueprint Medicines drug portfolio — 9 indexed compounds with therapeutic class and molecular targets from public FDA and regional approval metadata.

Drug portfolio

9 compounds
  1. avapritinib

    Antineoplastic and immunomodulating agents (L01)

    US regulatory status: approved. Molecular target: Platelet-derived growth factor receptor alpha.

    Target
    Platelet-derived growth factor receptor alpha
    Mechanism
    Stem cell growth factor receptor inhibitor
  2. azacitidine

    Antineoplastic and immunomodulating agents (L01)

    US regulatory status: approved. Molecular target: DNA (cytosine-5)-methyltransferase 1.

    Target
    DNA (cytosine-5)-methyltransferase 1
    Mechanism
    DNA (cytosine-5)-methyltransferase 3A inhibitor
  3. Development asset linked to Blueprint Medicines in public FDA and regional records.

  4. US regulatory status: approved. Molecular target: Copper.

    Target
    Copper
    Mechanism
    Copper chelating agent
  5. Development asset linked to Blueprint Medicines in public FDA and regional records.

  6. Development asset linked to Blueprint Medicines in public FDA and regional records.

  7. Development asset linked to Blueprint Medicines in public FDA and regional records.

  8. US regulatory status: approved. Molecular target: Bacterial penicillin-binding protein.

    Target
    Bacterial penicillin-binding protein
    Mechanism
    Bacterial penicillin-binding protein inhibitor
  9. US regulatory status: approved. Molecular target: Lanosterol 14-alpha demethylase.

    Target
    Lanosterol 14-alpha demethylase
    Mechanism
    Cytochrome P450 51 inhibitor