Wednesday, July 8, 2026

pharma · Geographic Atrophy · Geographic Atrophy Secondary to Age-related Macular Degeneration · APLS

Genzyme Europe

Genzyme Europe is a pharma organization headquartered in WALTHAM, MA, NL. It trades on NYSE under ticker APLS. Primary therapeutic focus areas include Geographic Atrophy, Geographic Atrophy Secondary to Age-related Macul

Gooimeer 10, Naarden, None 1411 DD, NL, WALTHAM, MA HQ
1981 Founded
273 Employees
Public company Type
APLS · NYSE Ticker
Company details
Status
Public
HQ
Gooimeer 10, Naarden, None 1411 DD, NL, WALTHAM, MA
Founded
1981
Employees
273
Programs
20
Drugs
5
Patents
24
Clinical program

Pegcetacoplan

Phase 3 · small molecule · Paroxysmal Nocturnal Hemoglobinuria

Pegcetacoplan for Paroxysmal Nocturnal Hemoglobinuria is a Phase 3 program (small_molecule) at Apellis Europe B.V. with 2 ClinicalTrials.gov record(s).

← All Apellis Europe B.V. projects Phase 3 small molecule completed

Internal code APL2-CP-PNH-204

Full intelligence profile for this program is being prepared.

At a glance

Sponsor
Apellis Europe B.V.
Phase
Phase 3
Modality
small_molecule
Indication
Paroxysmal Nocturnal Hemoglobinuria
Status
completed
Trials
2