Gene Therapy
🇪🇺 EMA Page 2EMA news and analysis for pharmaceutical BD, investment, and market access · 12 articles on this page
Unlock global gene therapy market insights. Stay ahead on regulatory approvals, clinical trials, and investment opportunities in this cutting-edge biotech sector.
Showing 13–24 of 26 articles
Ray Therapeutics RTx-015 Receives EMA PRIME Designation for Retinitis Pigmentosa Treatment
EMA · 2 min
Oliver GrantSilexion Therapeutics Submits Phase 2/3 Trial Application for SIL204 KRAS-Targeted Pancreatic Cancer Treatment
2 min
Charlotte MeyerSolid Biosciences Receives European Orphan Drug Designation for SGT-003 Duchenne Muscular Dystrophy Treatment
2 min
Dr. Hannah O'ConnorBioPharma Clinical Trials: Gene Therapy, Obesity, and Oncology Updates
general · 5 min
Dr. Elena RossiEMA Issues Positive Opinion for Itvisma (Onasemnogene Abeparvovec) Gene Therapy for Spinal Muscular Atrophy
EMA · Spinal Muscular Atrophy (SMA) · 3 min
Matteo RicciRNA Therapy Clinical Trials Market Reaches $3.4 Billion as Personalized Medicine Drives Growth Through 2035
2 min
Sofia AlvarezCenter for Cancer and Blood Disorders Launches CAR T-Cell Therapy Program in Maryland, Expanding Community Access
FDA · 2 min
Sofia AlvarezISCT 2026: Cell & Gene Therapy Manufacturing Innovations in Dublin
manufacturing · 4 min
Dr. Elena RossiAllogene Therapeutics Expands Cemacabtagene Ansegedleucel Phase 2 ALPHA3 Trial to South Korea and Australia
2 min
Dr. Elena RossiAskBio's Ametefgene Parvec Enters Phase II Trial for Parkinson's Disease Gene Therapy
2 min
Prof. Marcus WebbEMA Recommends Adstiladrin Gene Therapy for Bladder Cancer Treatment in March 2026
EMA · 2 min
Prof. Marcus WebbGene Therapy Market to Reach $43.8 Billion by 2034 as CRISPR and AAV Technologies Drive 12.27% Annual Growth
2 min
Dr. Elena RossiExplore intelligence