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Friday, June 19, 2026

Gene Therapy

🇪🇺 EMA Page 2

EMA news and analysis for pharmaceutical BD, investment, and market access · 12 articles on this page

Unlock global gene therapy market insights. Stay ahead on regulatory approvals, clinical trials, and investment opportunities in this cutting-edge biotech sector.

Showing 13–24 of 26 articles

High impact NewsApr 29, 2026

Ray Therapeutics RTx-015 Receives EMA PRIME Designation for Retinitis Pigmentosa Treatment

EMA · 2 min

Oliver Grant
Critical impact NewsApr 29, 2026

Silexion Therapeutics Submits Phase 2/3 Trial Application for SIL204 KRAS-Targeted Pancreatic Cancer Treatment

2 min

Charlotte Meyer
High impact NewsApr 29, 2026

Solid Biosciences Receives European Orphan Drug Designation for SGT-003 Duchenne Muscular Dystrophy Treatment

2 min

Dr. Hannah O'Connor
High impact NewsApr 29, 2026

BioPharma Clinical Trials: Gene Therapy, Obesity, and Oncology Updates

general · 5 min

Dr. Elena Rossi
High impact NewsApr 25, 2026

EMA Issues Positive Opinion for Itvisma (Onasemnogene Abeparvovec) Gene Therapy for Spinal Muscular Atrophy

EMA · Spinal Muscular Atrophy (SMA) · 3 min

Matteo Ricci
High impact NewsApr 25, 2026

RNA Therapy Clinical Trials Market Reaches $3.4 Billion as Personalized Medicine Drives Growth Through 2035

2 min

Sofia Alvarez
High impact NewsApr 23, 2026

Center for Cancer and Blood Disorders Launches CAR T-Cell Therapy Program in Maryland, Expanding Community Access

FDA · 2 min

Sofia Alvarez
Critical impact NewsApr 22, 2026

ISCT 2026: Cell & Gene Therapy Manufacturing Innovations in Dublin

manufacturing · 4 min

Dr. Elena Rossi
High impact NewsApr 22, 2026

Allogene Therapeutics Expands Cemacabtagene Ansegedleucel Phase 2 ALPHA3 Trial to South Korea and Australia

2 min

Dr. Elena Rossi
High impact NewsApr 21, 2026

AskBio's Ametefgene Parvec Enters Phase II Trial for Parkinson's Disease Gene Therapy

2 min

Prof. Marcus Webb
High impact NewsApr 18, 2026

EMA Recommends Adstiladrin Gene Therapy for Bladder Cancer Treatment in March 2026

EMA · 2 min

Prof. Marcus Webb
High impact NewsApr 17, 2026

Gene Therapy Market to Reach $43.8 Billion by 2034 as CRISPR and AAV Technologies Drive 12.27% Annual Growth

2 min

Dr. Elena Rossi