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Friday, June 19, 2026

Gene Therapy News

🇪🇺 EMA

EMA breaking news and regulatory updates for BD, investors, and analysts

Showing 1–12 of 23 articles

Medium impact NewsMay 23, 2026

European Biotechs Innovate in Cell and Gene Therapy Manufacturing

gene therapy · 4 min

Dr. Elena Rossi
Medium impact NewsMay 21, 2026

First GLP-1 Gene Therapy Clinical Trial Approved in Europe

EMA · GLP-1 · 2 min

Dr. Elena Rossi
Critical impact NewsMay 11, 2026

ISCT 2026: EU Manufacturing Innovations Day 1 Roundup

manufacturing · 6 min

Dr. Elena Rossi
High impact NewsMay 4, 2026

CRISPR Therapeutics Reports Q1 2026 Results as CASGEVY Gene Therapy Gains Global Regulatory Approval

Hematology/Blood Disorders · 3 min

Matteo Ricci
High impact NewsMay 4, 2026

Krystal Biotech Reports Strong Q1 2026 Results with VYJUVEK Global Expansion and Two Registrational Studies Pending

2 min

Dr. Lukas Schneider
Critical impact NewsMay 4, 2026

Vertex CASGEVY Gene Therapy Reaches 60,000+ Eligible Patients Across 10 Countries as Q1 2026 Results Show Global Expansion

Hematology/Blood Disorders · 3 min

Sofia Alvarez
High impact NewsMay 1, 2026

Stoke Therapeutics Zorevunersen Shows Promise for Dravet Syndrome Treatment Ahead of Q1 2026 Results

2 min

Dr. Lukas Schneider
Critical impact NewsMay 1, 2026

uniQure AMT-130 Gene Therapy Advances Toward UK Approval for Huntington's Disease Treatment

2 min

Matteo Ricci
High impact NewsMay 1, 2026

EU Biopharma Clinical Trials: AI & Gene Therapy Surge

general · 12 min

Dr. Elena Rossi
High impact NewsApr 29, 2026

Ray Therapeutics RTx-015 Receives EMA PRIME Designation for Retinitis Pigmentosa Treatment

EMA · 2 min

Oliver Grant
Critical impact NewsApr 29, 2026

Silexion Therapeutics Submits Phase 2/3 Trial Application for SIL204 KRAS-Targeted Pancreatic Cancer Treatment

2 min

Charlotte Meyer
High impact NewsApr 29, 2026

Solid Biosciences Receives European Orphan Drug Designation for SGT-003 Duchenne Muscular Dystrophy Treatment

2 min

Dr. Hannah O'Connor