Gene Therapy News
🇪🇺 EMAEMA breaking news and regulatory updates for BD, investors, and analysts
Showing 1–12 of 23 articles
European Biotechs Innovate in Cell and Gene Therapy Manufacturing
gene therapy · 4 min
Dr. Elena RossiFirst GLP-1 Gene Therapy Clinical Trial Approved in Europe
EMA · GLP-1 · 2 min
Dr. Elena RossiISCT 2026: EU Manufacturing Innovations Day 1 Roundup
manufacturing · 6 min
Dr. Elena RossiCRISPR Therapeutics Reports Q1 2026 Results as CASGEVY Gene Therapy Gains Global Regulatory Approval
Hematology/Blood Disorders · 3 min
Matteo RicciKrystal Biotech Reports Strong Q1 2026 Results with VYJUVEK Global Expansion and Two Registrational Studies Pending
2 min
Dr. Lukas SchneiderVertex CASGEVY Gene Therapy Reaches 60,000+ Eligible Patients Across 10 Countries as Q1 2026 Results Show Global Expansion
Hematology/Blood Disorders · 3 min
Sofia AlvarezStoke Therapeutics Zorevunersen Shows Promise for Dravet Syndrome Treatment Ahead of Q1 2026 Results
2 min
Dr. Lukas SchneideruniQure AMT-130 Gene Therapy Advances Toward UK Approval for Huntington's Disease Treatment
2 min
Matteo RicciEU Biopharma Clinical Trials: AI & Gene Therapy Surge
general · 12 min
Dr. Elena RossiRay Therapeutics RTx-015 Receives EMA PRIME Designation for Retinitis Pigmentosa Treatment
EMA · 2 min
Oliver GrantSilexion Therapeutics Submits Phase 2/3 Trial Application for SIL204 KRAS-Targeted Pancreatic Cancer Treatment
2 min
Charlotte MeyerSolid Biosciences Receives European Orphan Drug Designation for SGT-003 Duchenne Muscular Dystrophy Treatment
2 min
Dr. Hannah O'ConnorExplore intelligence