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Intelligence · Clinical Pipeline

R&D Pipeline Programs

ClinicalTrials.gov programs linked to pharma sponsors — phase, modality, and trial IDs for BD and competitive intelligence.

Programs indexed
18,156
Companies
1,062
Drugs tracked
3,187

Quick answer

NovaPharmaNews tracks 18,156 pharmaceutical R&D pipeline programs sourced from ClinicalTrials.gov, linked to sponsor companies. Each profile includes development phase, modality, trial status, NCT identifiers, and indication text — searchable for business development and competitive intelligence.

91 results for “BioMarin International Limited” Clear

  1. PARP inhibitor BMN-673

    BioMarin International Limited

    Metastatic Cancer

    phase 1 small molecule completed

    1 trial

  2. Talazoparib

    BioMarin International Limited

    Childhood Solid Tumors

    phase 1 small molecule completed

    1 trial

  3. Tetrahydrobiopterin 10 mg/kg

    BioMarin International Limited

    Claudication, Intermittent

    phase 1 small molecule active

    1 trial

  4. sapropterin dihydrochloride (6R-BH4)

    BioMarin International Limited

    Pulmonary Arterial Hypertension

    phase 1 small molecule completed

    1 trial

  5. Aldurazyme (Recombinant Human Alpha-L-Iduronidase)

    BioMarin International Limited

    Mucopolysaccharidosis I

    approved mab completed

    3 trials

  6. BH4

    BioMarin International Limited

    Pku Phenylketonuria

    approved small molecule active

    1 trial

  7. Kuvan

    BioMarin International Limited

    Phenylketonuria (PKU)

    approved small molecule completed

    2 trials

  8. Kuvan®

    BioMarin International Limited

    Phenylketonuria

    approved small molecule completed

    2 trials

  9. Naglazyme

    BioMarin International Limited

    Mucopolysaccharidosis VI

    approved small molecule completed

    1 trial

  10. Pegvaliase

    BioMarin International Limited

    Phenylketonuria

    approved mab active

    1 trial

  11. RDD to Palynziq

    BioMarin International Limited

    Phenylketonuria

    approved small molecule active

    1 trial

  12. ROCTAVIAN 2 × 1013 vector genomes/mL solution for infusion

    BioMarin International Limited

    Hemophilia A

    approved small molecule active

    1 trial

  13. laronidase

    BioMarin International Limited

    Mucopolysaccharidosis I

    approved small molecule completed

    3 trials

  14. saproterin dihydrochloride

    BioMarin International Limited

    Phenylketonuria

    approved small molecule completed

    1 trial

  15. Kuvan

    BioMarin International Limited

    Heart Failure

    small molecule completed

    1 trial

  16. Naglazyme®

    BioMarin International Limited

    Maroteaux-Lamy Syndrome

    small molecule terminated

    1 trial

  17. Sapropterin

    BioMarin International Limited

    Hyperphenylalaninemia

    small molecule terminated

    1 trial

  18. laronidase

    BioMarin International Limited

    Cognitive Decline

    small molecule completed

    1 trial

  19. sapropterin dihydrochloride

    BioMarin International Limited

    Autism Spectrum Disorder

    small molecule completed

    1 trial

Frequently asked questions

What is the NovaPharmaNews pipeline directory?

It is a searchable index of 18,156 clinical development programs grouped by sponsor company, with phase (Phase 1–3), modality, trial status, and linked NCT IDs from ClinicalTrials.gov.

Where does pipeline data come from?

Program records are derived from ClinicalTrials.gov and linked to NovaPharmaNews company profiles. Trial status and phase reflect registry data at last sync — verify on ClinicalTrials.gov before investment or partnering decisions. See our data sources page for attribution.

How do I find pipeline programs by company or phase?

Use the search box to match program name, indication, company name, or slug. Results are ordered with late-stage (Phase 3) programs first. Open any row to view the full program profile under its sponsor company.

Data attribution and licensing: Data sources