🇺🇸 FDA
Pipeline program

UX003

UX003-CL203

Phase 3 small_molecule completed

Quick answer

UX003 for Sly Syndrome is a Phase 3 program (small_molecule) at Ultragenyx Pharmaceutical with 2 ClinicalTrials.gov record(s).

Program details

Company
Ultragenyx Pharmaceutical
Indication
Sly Syndrome
Phase
Phase 3
Modality
small_molecule
Status
completed

Clinical trials