🇺🇸 FDA
Pipeline program

GTX-102

GTX-102-CL301

Phase 3 small_molecule active

Quick answer

GTX-102 for Angelman Syndrome is a Phase 3 program (small_molecule) at Ultragenyx Pharmaceutical with 4 ClinicalTrials.gov record(s).

Program details

Company
Ultragenyx Pharmaceutical
Indication
Angelman Syndrome
Phase
Phase 3
Modality
small_molecule
Status
active

Clinical trials