BMN 701
701-301
Phase 3 small_molecule terminated
Quick answer
BMN 701 for Late-onset Pompe Disease is a Phase 3 program (small_molecule) at BIOMARIN PHARMACEUTICAL INC with 1 ClinicalTrials.gov record(s).
Program details
- Company
- BIOMARIN PHARMACEUTICAL INC
- Indication
- Late-onset Pompe Disease
- Phase
- Phase 3
- Modality
- small_molecule
- Status
- terminated