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Intelligence · Clinical Pipeline

R&D Pipeline Programs

ClinicalTrials.gov programs linked to pharma sponsors — phase, modality, and trial IDs for BD and competitive intelligence.

Programs indexed
18,156
Companies
1,062
Drugs tracked
3,385

Quick answer

NovaPharmaNews tracks 18,156 pharmaceutical R&D pipeline programs sourced from ClinicalTrials.gov, linked to sponsor companies. Each profile includes development phase, modality, trial status, NCT identifiers, and indication text — searchable for business development and competitive intelligence.

91 results for “BioMarin” Clear

  1. Aldurazyme

    BioMarin International Limited

    Mucopolysaccharidosis I

    phase 3 mab completed

    1 trial

  2. BMN 110

    BioMarin International Limited

    Mucopolysaccharidosis IVA (Morquio A Syndrome)

    phase 3 small molecule completed

    1 trial

  3. BMN 110 - Weekly

    BioMarin International Limited

    Mucopolysaccharidosis IV A

    phase 3 small molecule completed

    1 trial

  4. BMN 110 Weekly

    BioMarin International Limited

    MPS IV A

    phase 3 small molecule completed

    1 trial

  5. BMN 111

    BioMarin International Limited

    Achondroplasia

    phase 3 small molecule active

    6 trials

  6. BMN 165

    BioMarin International Limited

    Phenylketonuria

    phase 3 small molecule completed

    1 trial

  7. BMN 333

    BioMarin International Limited

    Achondroplasia

    phase 3 small molecule active

    1 trial

  8. BMN 333, Voxzogo 0.56 mg powder and solvent for solution for injection, Voxzogo 1.2 mg powder and solvent for solution for injection, BMN 333

    BioMarin International Limited

    Achondroplasia

    phase 3 small molecule active

    1 trial

  9. BMN 701

    BioMarin International Limited

    Late-onset Pompe Disease

    phase 3 small molecule terminated

    1 trial

  10. BMN165 20mg/day

    BioMarin International Limited

    Phenylketonuria (PKU)

    phase 3 small molecule completed

    1 trial

  11. Drisapersen

    BioMarin International Limited

    Muscular Dystrophies

    phase 3 small molecule terminated

    2 trials

  12. INZ-701

    BioMarin International Limited

    Ectonucleotide Pyrophosphatase/phosphodiesterase1 Deficiency

    phase 3 small molecule active

    2 trials

  13. Kuvan®

    BioMarin International Limited

    Autistic Disorder

    phase 3 small molecule completed

    1 trial

  14. N-acetylgalactosamine 4-sulfatase

    BioMarin International Limited

    Mucopolysaccharidosis VI

    phase 3 small molecule completed

    3 trials

  15. Palynziq 2.5 mg solution for injection in pre-filled syringe, Palynziq 20 mg solution for injection in pre-filled syringe, Palynziq 10 mg solution for injection in pre-filled syringe

    BioMarin International Limited

    Phenylketonuria (PKU)

    phase 3 small molecule active

    1 trial

  16. Pegvaliase

    BioMarin International Limited

    Phenylketonuria (PKU)

    phase 3 small molecule active

    2 trials

  17. Placebo

    BioMarin International Limited

    Mucopolysaccharidosis VI

    phase 3 small molecule completed

    1 trial

  18. Sapropterin Dihydrochloride

    BioMarin International Limited

    Phenylketonurias

    phase 3 small molecule completed

    3 trials

  19. Sapropterin dihydrochloride

    BioMarin International Limited

    Phenylketonuria

    phase 3 small molecule completed

    4 trials

  20. Vosoritide

    BioMarin International Limited

    Hypochondroplasia

    phase 3 small molecule active

    3 trials

  21. Voxzogo 0.4 mg powder and solvent for solution for injection, Voxzogo 0.56 mg powder and solvent for solution for injection, Voxzogo 1.2 mg powder and solvent for solution for injection

    BioMarin International Limited

    Hypochondroplasia

    phase 3 small molecule active

    1 trial

  22. Voxzogo 1.2 mg powder and solvent for solution for injection, Voxzogo 0.4 mg powder and solvent for solution for injection, Voxzogo 0.56 mg powder and solvent for solution for injection

    BioMarin International Limited

    Achondroplasia

    phase 3 small molecule active

    1 trial

  23. Voxzogo 1.2 mg powder and solvent for solution for injection, powder and solvent for solution for injection, Voxzogo 0.56 mg powder and solvent for solution for injection

    BioMarin International Limited

    Hypochondroplasia

    phase 3 small molecule active

    1 trial

  24. rhIDU (recombinant human-Alpha-L-Iduronidase)

    BioMarin International Limited

    Mucopolysaccharidosis I

    phase 3 mab completed

    1 trial

Frequently asked questions

What is the NovaPharmaNews pipeline directory?

It is a searchable index of 18,156 clinical development programs grouped by sponsor company, with phase (Phase 1–3), modality, trial status, and linked NCT IDs from ClinicalTrials.gov.

Where does pipeline data come from?

Program records are derived from ClinicalTrials.gov and linked to NovaPharmaNews company profiles. Trial status and phase reflect registry data at last sync — verify on ClinicalTrials.gov before investment or partnering decisions. See our data sources page for attribution.

How do I find pipeline programs by company or phase?

Use the search box to match program name, indication, company name, or slug. Results are ordered with late-stage (Phase 3) programs first. Open any row to view the full program profile under its sponsor company.

Data attribution and licensing: Data sources