🇺🇸 FDA

Intelligence · Clinical Pipeline

R&D Pipeline Programs

ClinicalTrials.gov programs linked to pharma sponsors — phase, modality, and trial IDs for BD and competitive intelligence.

Programs indexed
18,156
Companies
1,062
Drugs tracked
3,385

Quick answer

NovaPharmaNews tracks 18,156 pharmaceutical R&D pipeline programs sourced from ClinicalTrials.gov, linked to sponsor companies. Each profile includes development phase, modality, trial status, NCT identifiers, and indication text — searchable for business development and competitive intelligence.

201 results for “Ultragenyx” Clear

  1. SDZ MSL-109

    Ultragenyx UK Limited

    Cytomegalovirus Infections

    phase 2 small molecule completed

    1 trial

  2. Sialic Acid Extended Release (SA-ER)

    Ultragenyx UK Limited

    GNE Myopathy

    phase 2 small molecule completed

    1 trial

  3. Sirolimus

    Ultragenyx UK Limited

    Anemia, Aplastic

    phase 2 small molecule active

    1 trial

  4. Sirolimus 0.5 mg

    Ultragenyx UK Limited

    Beta-Thalassemia

    phase 2 small molecule active

    2 trials

  5. Sodium Benzoate

    Ultragenyx UK Limited

    Amino Acid Metabolism, Inborn Errors

    phase 2 small molecule completed

    1 trial

  6. Sodium Phenylbutyrate

    Ultragenyx UK Limited

    Argininosuccinic Aciduria

    phase 2 small molecule completed

    1 trial

  7. Surgery

    Ultragenyx UK Limited

    Spastic Diplegia

    phase 2 other active

    1 trial

  8. Tiratricol

    Ultragenyx UK Limited

    Allan-Herndon-Dudley Syndrome

    phase 2 small molecule active

    1 trial

  9. Tridecanoic Acid

    Ultragenyx UK Limited

    Rett Syndrome

    phase 2 small molecule active

    1 trial

  10. Triheptanoin

    Ultragenyx UK Limited

    Tarui Disease

    phase 2 small molecule completed

    1 trial

  11. Triheptanoin

    Ultragenyx UK Limited

    Medium-chain Acyl-CoA Dehydrogenase Deficiency

    phase 2 small molecule active

    2 trials

  12. Triheptanoin

    Ultragenyx UK Limited

    Adult Polyglucosan Body Disease

    phase 2 small molecule completed

    1 trial

  13. Triheptanoin

    Ultragenyx UK Limited

    Glycogen Storage Disease Type V

    phase 2 small molecule completed

    1 trial

  14. Triheptanoin

    Ultragenyx UK Limited

    Glucose Transporter Type-1 Deficiency Syndrome (Glut1 DS)

    phase 2 small molecule completed

    1 trial

  15. Triheptanoin

    Ultragenyx UK Limited

    Glucose Transporter Type 1 Deficiency Syndrome

    phase 2 small molecule active

    1 trial

  16. Triheptanoin

    Ultragenyx UK Limited

    ALS

    phase 2 small molecule completed

    1 trial

  17. Triheptanoin oil

    Ultragenyx UK Limited

    Huntington Disease

    phase 2 small molecule completed

    1 trial

  18. UX003

    Ultragenyx UK Limited

    Mucopolysaccharidosis Type 7

    phase 2 small molecule completed

    1 trial

  19. UX007

    Ultragenyx UK Limited

    Glucose Transporter Type 1 Deficiency Syndrome

    phase 2 small molecule terminated

    1 trial

  20. UX007

    Ultragenyx UK Limited

    Long-chain Fatty Acid Oxidation Disorders (LC-FAOD)

    phase 2 small molecule completed

    1 trial

  21. UX007

    Ultragenyx UK Limited

    Carnitine Palmitoyltransferase (CPT I or CPT II) Deficiency

    phase 2 small molecule completed

    1 trial

  22. UX016

    Ultragenyx UK Limited

    GNE Myopathy

    phase 2 small molecule active

    1 trial

  23. UX053

    Ultragenyx UK Limited

    Glycogen Storage Disease Type III

    phase 2 mab terminated

    1 trial

  24. UX701

    Ultragenyx UK Limited

    Wilson Disease

    phase 2 gene therapy active

    1 trial

Frequently asked questions

What is the NovaPharmaNews pipeline directory?

It is a searchable index of 18,156 clinical development programs grouped by sponsor company, with phase (Phase 1–3), modality, trial status, and linked NCT IDs from ClinicalTrials.gov.

Where does pipeline data come from?

Program records are derived from ClinicalTrials.gov and linked to NovaPharmaNews company profiles. Trial status and phase reflect registry data at last sync — verify on ClinicalTrials.gov before investment or partnering decisions. See our data sources page for attribution.

How do I find pipeline programs by company or phase?

Use the search box to match program name, indication, company name, or slug. Results are ordered with late-stage (Phase 3) programs first. Open any row to view the full program profile under its sponsor company.

Data attribution and licensing: Data sources