Intelligence Β· Clinical Pipeline
R&D Pipeline Programs
ClinicalTrials.gov programs linked to pharma sponsors β phase, modality, and trial IDs for BD and competitive intelligence.
- Programs indexed
- 18,156
- Companies
- 1,062
- Drugs tracked
- 3,385
Quick answer
NovaPharmaNews tracks 18,156 pharmaceutical R&D pipeline programs sourced from ClinicalTrials.gov, linked to sponsor companies. Each profile includes development phase, modality, trial status, NCT identifiers, and indication text β searchable for business development and competitive intelligence.
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CASIMERSEN (SRP-4045), GOLODIRSEN (SRP-4053), 0,9% sodium chloride
Sarepta Therapeutics
Patients with Duchenne Muscular Dystrophy Amenable to Exon 45 or 53 Skipping.
1 trial -
Casimersen
Sarepta Therapeutics
Duchenne Muscular Dystrophy
1 trial -
Delandistrogene moxeparvovec-rokl
Sarepta Therapeutics
Duchenne Muscular Dystrophy
1 trial -
ETEPLIRSEN (AVI-4658)
Sarepta Therapeutics
Duchenne Muscular Dystrophy
1 trial -
Eteplirsen
Sarepta Therapeutics
Muscular Dystrophy, Duchenne
2 trials -
PREDNISONE, SRP-9003, PREDNISONE, PREDNISONE
Sarepta Therapeutics
Limb-girdle muscular dystrophy, type 2E/R4 (LGMD2E/R4) or Ξ²-sarcoglycanopathy
1 trial -
SRP-4045
Sarepta Therapeutics
Duchenne Muscular Dystrophy
2 trials -
SRP-9003
Sarepta Therapeutics
Limb-girdle Muscular Dystrophy
2 trials -
SRP-9005
Sarepta Therapeutics
Muscular Dystrophies, Limb-Girdle
1 trial -
Saline, 0.9% sodium chloride solution IV infusion marketed authorized will be used as the placebo and will be supplied by the site. the SmPC previously authorized are Country specific. for Belgium, Spain and Sweden per local requirements under CTDs no SmPCs were submitted., Delandistrogene moxeparvovec-rokl
Sarepta Therapeutics
Duchenne Muscular Dystrophy
1 trial -
delandistrogene moxeparvovec
Sarepta Therapeutics
Duchenne Muscular Dystrophy
7 trials -
eteplirsen
Sarepta Therapeutics
Duchenne Muscular Dystrophy (DMD)
2 trials -
AVI-4065 Injection
Sarepta Therapeutics
Hepatitis C
1 trial -
AVI-4658 (Eteplirsen)
Sarepta Therapeutics
Duchenne Muscular Dystrophy
1 trial -
AVI-4658 (Eteplirsen)
Sarepta Therapeutics
Duchenne Muscular Dystrophy (DMD)
1 trial -
AVI-4658 (PMO)
Sarepta Therapeutics
Duchenne Muscular Dystrophy
1 trial -
AVI-4658 for Injection
Sarepta Therapeutics
Duchenne Muscular Dystrophy
1 trial -
AVI-5126
Sarepta Therapeutics
Cardiovascular Disease
1 trial -
Amondys 45
Sarepta Therapeutics
Duchenne Muscular Dystrophy
1 trial -
Eteplirsen
Sarepta Therapeutics
Duchenne Muscular Dystrophy
2 trials -
Placebo
Sarepta Therapeutics
Duchenne Muscular Dystrophy
1 trial -
Placebo - Sodium Chloride 9 mg/ml (0.9%) - Solution for injection, ARO-DM1
Sarepta Therapeutics
Type 1 Myotonic Dystrophy
1 trial -
RESTEN-MP
Sarepta Therapeutics
Coronary Artery Disease
2 trials -
SODIUM CHLORIDE, ARO-DUX4
Sarepta Therapeutics
Facioscapulohumeral muscular dystrophy (FSHD)
1 trial
Frequently asked questions
What is the NovaPharmaNews pipeline directory?
It is a searchable index of 18,156 clinical development programs grouped by sponsor company, with phase (Phase 1β3), modality, trial status, and linked NCT IDs from ClinicalTrials.gov.
Where does pipeline data come from?
Program records are derived from ClinicalTrials.gov and linked to NovaPharmaNews company profiles. Trial status and phase reflect registry data at last sync β verify on ClinicalTrials.gov before investment or partnering decisions. See our data sources page for attribution.
How do I find pipeline programs by company or phase?
Use the search box to match program name, indication, company name, or slug. Results are ordered with late-stage (Phase 3) programs first. Open any row to view the full program profile under its sponsor company.
Data attribution and licensing: Data sources