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Intelligence · Clinical Pipeline

R&D Pipeline Programs

ClinicalTrials.gov programs linked to pharma sponsors — phase, modality, and trial IDs for BD and competitive intelligence.

Programs indexed
18,156
Companies
1,062
Drugs tracked
3,385

Quick answer

NovaPharmaNews tracks 18,156 pharmaceutical R&D pipeline programs sourced from ClinicalTrials.gov, linked to sponsor companies. Each profile includes development phase, modality, trial status, NCT identifiers, and indication text — searchable for business development and competitive intelligence.

201 results for “Ultragenyx” Clear

  1. Osilodrostat (Isturisa)

    Ultragenyx UK Limited

    Mild Autonomous Cortisol Secretion (MACS)

    approved small molecule active

    1 trial

  2. epoprostenol

    Ultragenyx UK Limited

    Hypertension, Pulmonary

    approved small molecule completed

    1 trial

  3. miglustat

    Ultragenyx UK Limited

    GM1 Gangliosidoses

    approved small molecule terminated

    1 trial

  4. Betaine

    Ultragenyx UK Limited

    Angelman Syndrome

    small molecule completed

    1 trial

  5. Blood sample

    Ultragenyx UK Limited

    Amelogenesis Imperfecta

    mab active

    1 trial

  6. Cyclophosphamide

    Ultragenyx UK Limited

    Systemic Lupus Erythematosus

    small molecule completed

    1 trial

  7. Estrogen

    Ultragenyx UK Limited

    Turner's Syndrome

    small molecule completed

    1 trial

  8. Intrathecal recombinant human alpha iduronidase

    Ultragenyx UK Limited

    Mucopolysaccharidosis I

    small molecule terminated

    1 trial

  9. Multistrain Probiotic

    Ultragenyx UK Limited

    Cystic Fibrosis in Children

    other active

    1 trial

  10. Neo-ASA

    Ultragenyx UK Limited

    Argininosuccinate Lyase Deficiency

    other completed

    1 trial

  11. Protein intake

    Ultragenyx UK Limited

    Phenylketonuria

    other completed

    1 trial

  12. anti-thymocyte globulin

    Ultragenyx UK Limited

    Purpura, Schoenlein-Henoch

    small molecule active

    1 trial

  13. anti-thymocyte globulin

    Ultragenyx UK Limited

    Neutropenia

    small molecule completed

    1 trial

  14. anti-thymocyte globulin

    Ultragenyx UK Limited

    Graft Versus Host Disease

    small molecule active

    1 trial

  15. anti-thymocyte globulin

    Ultragenyx UK Limited

    Immunologic Deficiency Syndromes

    small molecule terminated

    1 trial

  16. anti-thymocyte globulin

    Ultragenyx UK Limited

    Chediak-Higashi Syndrome

    small molecule active

    1 trial

  17. botulinum toxin type A

    Ultragenyx UK Limited

    Hyperhidrosis

    small molecule completed

    1 trial

  18. calcitriol

    Ultragenyx UK Limited

    Psoriasis

    small molecule completed

    1 trial

  19. clomiphene citrate

    Ultragenyx UK Limited

    Hyperinsulinism

    small molecule completed

    1 trial

  20. cyclophosphamide

    Ultragenyx UK Limited

    Fanconi's Anemia

    small molecule completed

    2 trials

  21. cyclosporine

    Ultragenyx UK Limited

    Metabolism, Inborn Errors

    small molecule completed

    1 trial

  22. dextromethorphan

    Ultragenyx UK Limited

    Rett Syndrome

    small molecule completed

    1 trial

  23. droxidopa

    Ultragenyx UK Limited

    Shy-Drager Syndrome

    small molecule completed

    1 trial

  24. enalapril

    Ultragenyx UK Limited

    IGA Glomerulonephritis

    small molecule completed

    1 trial

Frequently asked questions

What is the NovaPharmaNews pipeline directory?

It is a searchable index of 18,156 clinical development programs grouped by sponsor company, with phase (Phase 1–3), modality, trial status, and linked NCT IDs from ClinicalTrials.gov.

Where does pipeline data come from?

Program records are derived from ClinicalTrials.gov and linked to NovaPharmaNews company profiles. Trial status and phase reflect registry data at last sync — verify on ClinicalTrials.gov before investment or partnering decisions. See our data sources page for attribution.

How do I find pipeline programs by company or phase?

Use the search box to match program name, indication, company name, or slug. Results are ordered with late-stage (Phase 3) programs first. Open any row to view the full program profile under its sponsor company.

Data attribution and licensing: Data sources