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Intelligence · Clinical Pipeline

R&D Pipeline Programs

ClinicalTrials.gov programs linked to pharma sponsors — phase, modality, and trial IDs for BD and competitive intelligence.

Programs indexed
18,156
Companies
1,062
Drugs tracked
3,385

Quick answer

NovaPharmaNews tracks 18,156 pharmaceutical R&D pipeline programs sourced from ClinicalTrials.gov, linked to sponsor companies. Each profile includes development phase, modality, trial status, NCT identifiers, and indication text — searchable for business development and competitive intelligence.

201 results for “Ultragenyx UK Limited” Clear

  1. ANAWIDOW [antivenin latrodectus (black widow) equine immune F(ab)2] lyophilized powder for solution 10 mL

    Ultragenyx UK Limited

    Latrodectism

    phase 1 small molecule completed

    1 trial

  2. Acetazolamide

    Ultragenyx UK Limited

    Andersen-Tawil Syndrome

    phase 1 small molecule terminated

    1 trial

  3. Ad5-CB-CFTR

    Ultragenyx UK Limited

    Cystic Fibrosis

    phase 1 gene therapy completed

    1 trial

  4. Burosumab

    Ultragenyx UK Limited

    Cutaneous Skeletal Hypophosphatemia Syndrome (CSHS)

    phase 1 small molecule active

    1 trial

  5. CRD-TMH-001

    Ultragenyx UK Limited

    Duchenne Muscular Dystrophy

    phase 1 small molecule active

    1 trial

  6. H5.001CBCFTR

    Ultragenyx UK Limited

    Cystic Fibrosis

    phase 1 gene therapy completed

    1 trial

  7. ManNAc

    Ultragenyx UK Limited

    Hereditary Inclusion Body Myopathy (HIBM)

    phase 1 small molecule completed

    1 trial

  8. N-acetylcysteine

    Ultragenyx UK Limited

    Parkinson's Disease

    phase 1 small molecule completed

    1 trial

  9. Sargramostim

    Ultragenyx UK Limited

    Autoimmune Pulmonary Alveolar Proteinosis

    phase 1 small molecule completed

    1 trial

  10. Sialic Acid Extended Release (SA-ER) Tablets

    Ultragenyx UK Limited

    Hereditary Inclusion Body Myopathy (HIBM)

    phase 1 small molecule completed

    1 trial

  11. Triheptanoin

    Ultragenyx UK Limited

    Glycogen Storage Disease Type I

    phase 1 small molecule completed

    1 trial

  12. Triheptanoin

    Ultragenyx UK Limited

    Pyruvate Dehydrogenase Complex Deficiency

    phase 1 small molecule active

    1 trial

  13. amifostine

    Ultragenyx UK Limited

    Fanconi's Anemia

    phase 1 small molecule active

    1 trial

  14. anti-thymocyte globulin

    Ultragenyx UK Limited

    Systemic Lupus Erythematosus

    phase 1 small molecule active

    1 trial

  15. anti-thymocyte globulin

    Ultragenyx UK Limited

    Multiple Sclerosis

    phase 1 small molecule completed

    1 trial

  16. colchicine

    Ultragenyx UK Limited

    Cirrhosis

    phase 1 small molecule active

    1 trial

  17. cyclophosphamide

    Ultragenyx UK Limited

    Multiple Sclerosis

    phase 1 small molecule completed

    1 trial

  18. filgrastim

    Ultragenyx UK Limited

    Fanconi's Anemia

    phase 1 small molecule active

    1 trial

  19. gene therapy

    Ultragenyx UK Limited

    Familial Hypercholesterolemia

    phase 1 other completed

    1 trial

  20. monoclonal antibody M-T412

    Ultragenyx UK Limited

    Multiple Sclerosis

    phase 1 small molecule completed

    1 trial

  21. recombinant adenovirus containing the ornithine transcarbamylase gene

    Ultragenyx UK Limited

    Ornithine Transcarbamylase Deficiency Disease

    phase 1 gene therapy terminated

    1 trial

  22. von Willebrand factor

    Ultragenyx UK Limited

    Von Willebrand's Disease

    phase 1 small molecule completed

    1 trial

  23. Crysvita (burosumab-twza) Treatment

    Ultragenyx UK Limited

    Epidermal Nevus Syndrome

    approved small molecule completed

    1 trial

  24. Leucovorin calcium

    Ultragenyx UK Limited

    Toxoplasmosis

    approved small molecule active

    1 trial

Frequently asked questions

What is the NovaPharmaNews pipeline directory?

It is a searchable index of 18,156 clinical development programs grouped by sponsor company, with phase (Phase 1–3), modality, trial status, and linked NCT IDs from ClinicalTrials.gov.

Where does pipeline data come from?

Program records are derived from ClinicalTrials.gov and linked to NovaPharmaNews company profiles. Trial status and phase reflect registry data at last sync — verify on ClinicalTrials.gov before investment or partnering decisions. See our data sources page for attribution.

How do I find pipeline programs by company or phase?

Use the search box to match program name, indication, company name, or slug. Results are ordered with late-stage (Phase 3) programs first. Open any row to view the full program profile under its sponsor company.

Data attribution and licensing: Data sources