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Intelligence · Clinical Pipeline

R&D Pipeline Programs

ClinicalTrials.gov programs linked to pharma sponsors — phase, modality, and trial IDs for BD and competitive intelligence.

Programs indexed
18,156
Companies
1,062
Drugs tracked
3,385

Quick answer

NovaPharmaNews tracks 18,156 pharmaceutical R&D pipeline programs sourced from ClinicalTrials.gov, linked to sponsor companies. Each profile includes development phase, modality, trial status, NCT identifiers, and indication text — searchable for business development and competitive intelligence.

201 results for “Ultragenyx” Clear

  1. soy protein isolate

    Ultragenyx UK Limited

    Hereditary Hemorrhagic Telangiectasia

    phase 3 small molecule completed

    1 trial

  2. topiramate

    Ultragenyx UK Limited

    Lennox-Gastaut Syndrome

    phase 3 small molecule completed

    1 trial

  3. whole-cell pertussis vaccine

    Ultragenyx UK Limited

    Pertussis

    phase 3 mab completed

    1 trial

  4. -aminosalicylic acid

    Ultragenyx UK Limited

    Ulcerative Colitis

    phase 2 small molecule completed

    1 trial

  5. AVTX-801

    Ultragenyx UK Limited

    SLC35A2-CDG - Solute Carrier Family 35 Member A2 Congenital Disorder of Glycosylation

    phase 2 small molecule active

    1 trial

  6. Abatacept

    Ultragenyx UK Limited

    Wegener's Granulomatosis

    phase 2 small molecule completed

    1 trial

  7. Abatacept

    Ultragenyx UK Limited

    Takayasu's Arteritis

    phase 2 small molecule completed

    1 trial

  8. Aceneuramic Acid Extended-Release

    Ultragenyx UK Limited

    Hereditary Inclusion Body Myopathy

    phase 2 small molecule terminated

    1 trial

  9. Antithymocyte globulin (ATG)

    Ultragenyx UK Limited

    Myelodysplastic Syndrome

    phase 2 small molecule active

    1 trial

  10. BPS804

    Ultragenyx UK Limited

    Osteogenesis Imperfecta

    phase 2 small molecule completed

    1 trial

  11. Cisplatin

    Ultragenyx UK Limited

    Squamous Cell Carcinoma of the Anus

    phase 2 small molecule active

    1 trial

  12. Colchicine

    Ultragenyx UK Limited

    Primary Cutaneous Vasculitis

    phase 2 small molecule active

    1 trial

  13. DTX101

    Ultragenyx UK Limited

    Hemophilia B

    phase 2 gene therapy terminated

    1 trial

  14. DTX401

    Ultragenyx UK Limited

    GSD1

    phase 2 gene therapy completed

    1 trial

  15. Exercise

    Ultragenyx UK Limited

    Spinal Cord Injury

    phase 2 other completed

    1 trial

  16. GLUT1 DS

    Ultragenyx UK Limited

    Glut1 Deficiency Syndrome

    phase 2 small molecule completed

    1 trial

  17. Hydroxyproline and Leucine

    Ultragenyx UK Limited

    Hyperoxaluria

    phase 2 small molecule completed

    1 trial

  18. Losartan Potassium

    Ultragenyx UK Limited

    Eosinophilic Esophagitis

    phase 2 small molecule completed

    1 trial

  19. Melphalan

    Ultragenyx UK Limited

    Amyloidosis

    phase 2 small molecule completed

    1 trial

  20. N-acetylcysteine

    Ultragenyx UK Limited

    Gaucher Disease Type 1

    phase 2 small molecule completed

    1 trial

  21. NTBC

    Ultragenyx UK Limited

    Tyrosinemia, Type I

    phase 2 small molecule completed

    1 trial

  22. POST Triheptanoin

    Ultragenyx UK Limited

    Frontal Lobe Hypometabolism

    phase 2 small molecule completed

    1 trial

  23. RAD001

    Ultragenyx UK Limited

    PTEN Gene Mutation

    phase 2 small molecule completed

    1 trial

  24. SA-ER 500 mg

    Ultragenyx UK Limited

    GNE Myopathy

    phase 2 small molecule completed

    1 trial

Frequently asked questions

What is the NovaPharmaNews pipeline directory?

It is a searchable index of 18,156 clinical development programs grouped by sponsor company, with phase (Phase 1–3), modality, trial status, and linked NCT IDs from ClinicalTrials.gov.

Where does pipeline data come from?

Program records are derived from ClinicalTrials.gov and linked to NovaPharmaNews company profiles. Trial status and phase reflect registry data at last sync — verify on ClinicalTrials.gov before investment or partnering decisions. See our data sources page for attribution.

How do I find pipeline programs by company or phase?

Use the search box to match program name, indication, company name, or slug. Results are ordered with late-stage (Phase 3) programs first. Open any row to view the full program profile under its sponsor company.

Data attribution and licensing: Data sources