🇺🇸 FDA
Pipeline program

RB001

RB001-101

Unknown gene_therapy active

Quick answer

RB001 for Phelan-McDermid Syndrome is a Unknown program (gene_therapy) at First Tracks Biotherapeutics with 1 ClinicalTrials.gov record(s).

Program details

Company
First Tracks Biotherapeutics
Indication
Phelan-McDermid Syndrome
Phase
Unknown
Modality
gene_therapy
Status
active

Clinical trials